Tag Archives: rare

Preschool teacher, 30, thriving after being given one week to live with rare brain tumor

Preschool teacher, 30, diagnosed with a rare brain tumor who was given one week to live in 2017 is thriving after taking a new clinical trial drug Amanda Thomas, 30, from Charlotte, North Carolina, went to the hospital in November 2017 after experiencing headaches following a car accident An MRI showed she had H3 K27M mutant… Read More »

The organization helping to bring new drugs for rare diseases to market

A research team has reason to celebrate after the Food and Drug Administration granted it approval on Friday to begin a clinical trial for a new pediatric brain cancer drug, one that might have ended up overlooked by pharmaceutical companies. The lead researcher on the team, Dr. Teresa Purzner has already beat impossible odds. The… Read More »